“There is no cure.” These words haunt millions of families whose children face a lifetime of incurable illness. While medications and surgical interventions can improve outcomes, these therapies are quickly reaching their limits.
But there is good news. In recent years, transformative cell and gene therapies have made it possible to not only treat but actually cure diseases.
In 2017, Stanford Medicine launched the Center for Definitive and Curative Medicine (CDCM) to conceive, test, refine, and prove incredible new therapies that will change the future of children’s health.
This week, CDCM faculty joined us for a virtual event, Curing the Incurable: Breakthrough Therapies Transforming the Future of Medicine, to share their grand vision and exciting advances on the horizon, including:
- the upcoming launch of the first ever in-human gene correction clinical trial, a potential cure for sickle cell disease
- the anticipated launch of a clinical trial this year for a cure for IPEX, a rare autoimmune disease
- continued refinement of a novel form of stem cell transplant pioneered by CDCM faculty that allows for safer and more effective treatment of patients without a donor match
Watch the video here:
Philanthropy is essential to accelerate groundbreaking research that can only be accomplished by these experts at Stanford. If you are interested in learning more about this work, please contact Payal Shah at Payal.Shah@lpfch.org.
Investments in this vision have the highest potential impact: helping millions of children around the world live without disease.
